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Nonclinical Evaluation Studies of Cellular and Gene Therapy Products

1,38878 LEI
1,54309 LEI
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Descriere

Nonclinical Evaluation Studies of Cellular and Gene Therapy Products: Strategies, Models, and Regulatory Frameworks

systematically explores the nonclinical evaluation of Cell and Gene Therapies (CGT) products, emphasizing risk mitigation and innovation.

The book provides comprehensive coverage, including 20+ chapters spanning preclinical toxicology, pharmacokinetics, and novel evaluation models.

It is the first book to integrate organ-on-chip models into CGT evaluation, reflecting FDA/NMPA modernization initiatives.

It includes practical guidance on addressing CRISPR off-target effects, immunogenicity, and long-term carcinogenicity risks.

Detalii
  • ISBN: 9780443486128
  • Autori: Quanjun Wang, Qingli Wang, Xingchao Geng
  • Limba: Engleză
  • An apariție: 2026
  • Coperta: Paperback
  • Editura: Elsevier Science
  • Nr. pagini: 650
  • Greutate: 450gr
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